Search Results
RettEd Webinar: Gene Therapy in Rare Disease
Introduction to gene-directed therapies (a LinkAGE webinar)
RettEd Webinar: Bringing Treatments & Cures Home
Gene Therapy for Rare Disorders: RAREfest20
GeneTx Webinar
The Promises and Pitfalls of Gene Therapy for Rare Diseases: Gene Therapy Case Study–IND Submission
RettEd: 2019 Research Update 20 Years Since the MECP2 Gene Discovery feat. Huda Y. Zoghbi, M.D.
Josie Godfrey. The challenge of rare diseases. 08.04.2021
Highlights from ESGCT 2021: gene therapy clinical data, advances in gene editing & AAV toxicity
Gene Replacement for Rett Syndrome 101 | Rett Syndrome Research Trust
RettEd: What is Rett Syndrome?
Rocketing Forward in Gene Therapy | SXSW 2021
